GS-100 shine mai ɗaukar hoto na AAV9 wanda ke yin lambar kwayar halittar NGLY1 ta mutum. Ya sami sunan magungunan marayu daga Hukumar Abinci da Magunguna ta Amurka da Hukumar Magunguna ta Turai (EMA) Hakanan maganin ya sami FDA's rare pediatric disease designation a cikin 2021 da kuma saurin saurin sauri a bara.