I-GS-100 yi-recombiant AAV9 vector encoding the human NGLY1 gene. Ifumene igama elithi orphan drug kwi-US Food and Drug Administration kunye ne-European Medicine Agency (EMA) Le ndlela yokunyanga iphinde yafumana igama elithi FDA's rare paediatric disease ngo-2021 kunye ne-fast track designation kunyaka ophelileyo.