GS-100 mooy benn benn AAV9 bu ñu boole ci gene NGLY1 bi ci nit. Jëf boobu am na ci li ñu naan " orphan drug " ci Amerig yi, ci wàllu ñam ak wal ak ci wàllu xaritaayu Europe yi (EMA). Jëf boobu am na ci li ñu naan " rare pediatric disease " ci FDA ci atum 2021 ak " fast track " ci atum 2021.