GS-100 ke rekombinant AAV9 vector e e tsentseng NGLY1 gene mo bathong. E amogetse leina la orphan drug go tswa go US Food and Drug Administration le European Medicine Agency (EMA). Kalafi e e amogetse gape leina la FDA la bolwetse jo bo sa tlwaelegang jwa bana ka 2021 le leina la fast track ngogola.