Ko te GS-100 he kaikawe AAV9 whakakotahi i te ira NGLY1 tangata. Kua riro i a ia te tohu rongoa pani mai i te US Food and Drug Administration me te European Medicine Agency (EMA) I whiwhi ano te rongoa i te tohu mate tamariki iti a te FDA i te tau 2021 me te tohu tere i tera tau.