GS-100 ni agakoko gakomoka kuri AAV9 gafite gene ya NGLY1 mu muntu. Byatumye ikoreshwa nk'umuti w'imfubyi n'ikigo cy'Amerika gishinzwe ibiribwa n'imiti n'ikigo cy'Uburayi gishinzwe imiti (EMA). Ubu buryo bwo kuvura bwahawe kandi FDA's rare paediatric disease designation mu 2021 no kwihutisha igenwa ry'umwaka ushize.