GS-100 bụ ihe na-agbanwe agbanwe AAV9 nke na-agbanwe mkpụrụ ndụ ihe nketa NGLY1 nke mmadụ. Ọ natara aha ọgwụ na-enweghị ọgwụ site na US Food and Drug Administration na European Medicine Agency (EMA) Usoro ọgwụgwọ ahụ nwetakwara aha FDA's rare paediatric disease na 2021 na aha ngwa ngwa afọ gara aga.