GS-100 ee raan ye AAV9 gene gene NGLY1 gene. Yen acï yök ke ye wal ye kɔc ke piny America ku jɔl ya European Medicine Agency (EMA) ye cɔl orphan drug. Ku jɔl ya FDA's rare paediatric disease designation në ruön de 2021 ku jɔl ya fast track designation në ruön cï lɔ.